Browsing by Author Mendonça, Liliana

Results 1 to 17 of 17
Issue DateTitleAuthor(s)TypeAccess
2023Editorial: Advanced (gene and cell) therapies for central nervous system applicationsMendonça, Liliana ; Webster, Christopher; Boltze, Johannes; Nóbrega, Clévio articleopenAccess
2023Editorial: Global excellence in gene and cell therapy: EuropeMendonça, Liliana ; Boltze, Johannes; Nóbrega, Clévio articleopenAccess
8-Oct-2019Establishment and Characterization of Human Pluripotent Stem Cells derived Brain OrganoidsBrás, João Pedro SantosmasterThesisembargoedAccess
13-Nov-2021Extracellular Vesicles Physiological Role and the Particular Case of Disease-Spreading Mechanisms in Polyglutamine DiseasesMoreira, Ricardo ; Mendonça, Liliana Simões ; Almeida, Luís Pereira de articleopenAccess
4-Dec-2020Impact of human iPSC-derived NESC transplantation in MJD-associated neuropathology and motor impairmentsVinhas, Ana Catarina Paulino do ÓmasterThesisembargoedAccess
3-Oct-2018Investigation of mutant ataxin-3 spreading in Machado-Joseph DiseaseMoreira, Ricardo Gomes masterThesisembargoedAccess
18-Sep-2018IPSCs-derived NESCs for Neuroregeneration in Machado-Joseph disease.Henriques, Daniel Alexandre Sousa masterThesisembargoedAccess
10-Aug-2020Lysosomal Storage Disease-Associated Neuropathy: Targeting Stable Nucleic Acid Lipid Particle (SNALP)-Formulated siRNAs to the Brain as a Therapeutic ApproachCoutinho, Maria Francisca; Santos, Juliana Inês; Mendonça, Liliana ; Matos, Liliana; Prata, Maria João ; Jurado, Amália ; Lima, Maria C. Pedroso de ; Alves, SandraarticleopenAccess
2016Motor Dysfunctions and Neuropathology in Mouse Models of Spinocerebellar Ataxia Type 2: A Comprehensive ReviewAlves-Cruzeiro, João M. da Conceição ; Mendonça, Liliana ; Almeida, Luís Pereira de articleopenAccess
31-May-2010Novel nanotechnological approaches for chronic myeloid leukemia treatment : molecular and cellular targeting for gene silencing of overexpressed genesMendonça, Liliana Simões doctoralThesisembargoedAccess
13-Sep-2019Patient-specific iPSC-derived NESC for Machado-Joseph Disease treatmentFernandes, Vanessa Alexandra CastanheiramasterThesisembargoedAccess
2019Restoring brain cholesterol turnover improves autophagy and has therapeutic potential in mouse models of spinocerebellar ataxiaNóbrega, Clévio David Rodrigues ; Mendonça, Liliana Simões ; Marcelo, Adriana Isabel do Vale ; Lamazière, Antonin; Tomé, Sandra Marisa Oliveira ; Despres, Gaetan; Matos, Carlos A; Mechmet, Fatich; Langui, Dominique; den Dunnen, Wilfred; Almeida, Luís Pereira de ; Cartier, Nathalie; Alves, Sandro José Paiva Fernandes articleembargoedAccess
Mar-2016Safety profile of the intravenous administration of brain-targeted stable nucleic acid lipid particlesConceição, Mariana ; Mendonça, Liliana ; Nóbrega, Clévio; Gomes, Célia ; Costa, Pedro ; Hirai, Hirokazu; Moreira, João Nuno ; Lima, Maria C. Pedroso de ; Manjunath, N.; Almeida, Luís Pereira de articleopenAccess
2019Successes and Hurdles in Stem Cells Application and Production for Brain TransplantationHenrique, Daniel ; Moreira, Ricardo ; Schwamborn, Jens; Almeida, Luís Pereira de ; Mendonça, Liliana articleopenAccess
1-Jun-2023The stress granule protein G3BP1 alleviates spinocerebellar ataxia-associated deficitsKoppenol, Rebekah; Conceição, André ; Afonso, Inês T.; Afonso-Reis, Ricardo; Costa, Rafael G.; Tomé, Sandra ; Teixeira, Diogo ; da Silva, Joana Pinto; Codêsso, José Miguel ; Brito, David V. C.; Mendonça, Liliana ; Marcelo, Adriana ; Almeida, Luís Pereira de ; Matos, Carlos A.; Nóbrega, Clévio articleopenAccess
2013Tumor-targeted Chlorotoxin-coupled Nanoparticles for Nucleic Acid Delivery to Glioblastoma Cells: A Promising System for Glioblastoma TreatmentCosta, Pedro M. ; Cardoso, Ana L. ; Mendonça, Liliana S. ; Serani, Angelo ; Custódia, Carlos ; Conceição, Mariana ; Simões, Sérgio ; Moreira, João N. ; Almeida, Luis Pereira de ; Lima, M. C. P. de articleopenAccess
11-Jul-2019Understanding how birds rebuild fat stores during migration: insights from an experimental studyAraújo, Pedro M. ; Viegas, Ivan ; Rocha, Afonso D.; Villegas, Auxiliadora; Jones, John G. ; Mendonça, Liliana ; Ramos, Jaime A. ; Masero, José A.; Alves, José A.articleopenAccess