Portuguese Society for Metabolic Disorders (Sociedade Portuguesa de Doenças Metabólicas, SPDM—Bolsa SPDM de apoio à investigação Dr Aguinaldo Cabral 2018 (2019DGH1629/SPDM2018I&D) and 2019 (2020DGH1834)),


Project title
Portuguese Society for Metabolic Disorders (Sociedade Portuguesa de Doenças Metabólicas, SPDM—Bolsa SPDM de apoio à investigação Dr Aguinaldo Cabral 2018 (2019DGH1629/SPDM2018I&D) and 2019 (2020DGH1834)),

Publications
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Issue DateTitleAuthor(s)TypeAccess
119-Apr-2022Splicing Modulation as a Promising Therapeutic Strategy for Lysosomal Storage Disorders: The Mucopolysaccharidoses ExampleSantos, Juliana Inês; Gonçalves, Mariana; Matos, Liliana; Moreira, Luciana ; Carvalho, Sofia; Prata, Maria João ; Coutinho, Maria Francisca; Alves, SandraarticleopenAccess