Browsing by Subject antisense oligonucleotides (ASOs)
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Issue Date | Title | Author(s) | Type | Access |
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19-Apr-2022 | Splicing Modulation as a Promising Therapeutic Strategy for Lysosomal Storage Disorders: The Mucopolysaccharidoses Example | Santos, Juliana Inês; Gonçalves, Mariana; Matos, Liliana; Moreira, Luciana ; Carvalho, Sofia; Prata, Maria João ; Coutinho, Maria Francisca; Alves, Sandra | article | openAccess |