Browsing by Subject antisense oligonucleotides (ASOs)

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Issue DateTitleAuthor(s)TypeAccess
19-Apr-2022Splicing Modulation as a Promising Therapeutic Strategy for Lysosomal Storage Disorders: The Mucopolysaccharidoses ExampleSantos, Juliana Inês; Gonçalves, Mariana; Matos, Liliana; Moreira, Luciana ; Carvalho, Sofia; Prata, Maria João ; Coutinho, Maria Francisca; Alves, SandraarticleopenAccess