Browsing by Subject lysosomal storage diseases (LSDs)
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| Issue Date | Title | Author(s) | Type | Access |
|---|---|---|---|---|
| 10-Aug-2020 | Lysosomal Storage Disease-Associated Neuropathy: Targeting Stable Nucleic Acid Lipid Particle (SNALP)-Formulated siRNAs to the Brain as a Therapeutic Approach | Coutinho, Maria Francisca; Santos, Juliana Inês; Mendonça, Liliana ; Matos, Liliana; Prata, Maria João ; Jurado, Amália ; Lima, Maria C. Pedroso de ; Alves, Sandra | article | openAccess |
| 19-Apr-2022 | Splicing Modulation as a Promising Therapeutic Strategy for Lysosomal Storage Disorders: The Mucopolysaccharidoses Example | Santos, Juliana Inês; Gonçalves, Mariana; Matos, Liliana; Moreira, Luciana ; Carvalho, Sofia; Prata, Maria João ; Coutinho, Maria Francisca; Alves, Sandra | article | openAccess |