Browsing by Subject Lysosomal Storage Diseases

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Issue DateTitleAuthor(s)TypeAccess
10-Aug-2020Lysosomal Storage Disease-Associated Neuropathy: Targeting Stable Nucleic Acid Lipid Particle (SNALP)-Formulated siRNAs to the Brain as a Therapeutic ApproachCoutinho, Maria Francisca; Santos, Juliana Inês; Mendonça, Liliana ; Matos, Liliana; Prata, Maria João ; Jurado, Amália ; Lima, Maria C. Pedroso de ; Alves, SandraarticleopenAccess