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Issue DateTitleAuthor(s)TypeAccess
17-Oct-2017Machado-Joseph Disease: Understanding Epidemiologic and Clinical Features and a Potential New Therapeutic EntitySilva, Patrick Joel da masterThesisembargoedAccess
2020Mesenchymal Stromal Cells' Therapy for Polyglutamine Disorders: Where Do We Stand and Where Should We Go?Barros, Inês ; Marcelo, Adriana ; Silva, Teresa P. ; Barata, João ; Ramos, António David Rufino ; Almeida, Luís P. de ; Miranda, Catarina O. articleopenAccess
16-Dec-2020MicroRNA profiling in human cell-based models of Machado-Joseph diseaseSantos, Maria Inês Nunes dosmasterThesisembargoedAccess
25-Jul-2013MicroRNAs as molecular targets for non-viral gene therapy of glioblastoma: development of a lipid-based nanosystem for nucleic acid delivery to brain tumor cellsCosta, Pedro Miguel Coutinho da doctoralThesisopenAccess
2-May-2017MicroRNAs targeting Ataxin-3 mRNA in Machado-Joseph disease: from pathogenesis to therapyCarmona, Vitor Manuel Martins doctoralThesisembargoedAccess
Sep-2016miRNAs como biomarcadores e como estratégias de intervenção terapêutica na doença de AlzheimerMarques, Ana Lúcia CarreiraotheropenAccess
2020Mitochondrial and Redox Modifications in Huntington Disease Induced Pluripotent Stem Cells Rescued by CRISPR/Cas9 CAGs TargetingLopes, Carla ; Tang, Yang; Anjo, Sandra I. ; Manadas, Bruno ; Onofre, Isabel ; Almeida, Luís P. de ; Daley, George Q; Schlaeger, Thorsten M; Rego, Ana Cristina Carvalho articleopenAccess
1997Modeling dissolution of sparingly soluble multisized powdersAlmeida, Luís Pereira de ; Simões, Sérgio ; Brito, Paulo ; Portugal, António ; Figueiredo, Margarida articleopenAccess
2013Modelo Genético da Doença de Parkinson baseado na sobreexpressão da alfa-sinucleínaAnjos, Vanessa masterThesisembargoedAccess
2014Modulating actin dynamics during axon formation, growth and regeneration : the role of AdducinTavares, Carla Anita GomesmasterThesisopenAccess
2014Multipotent mesenchymal stromal cells for Machado Joseph disease therapySilva, Teresa Maria Pereira da masterThesisopenAccess
7-Jul-2020Neurofilaments in spinocerebellar ataxia type 3: blood biomarkers at the preataxic and ataxic stage in humans and miceWilke, Carlo; Haas, Eva; Reetz, Kathrin; Faber, Jennifer; Garcia-Moreno, Hector; Santana, Magda M. ; van de Warrenburg, Bart; Hengel, Holger; Lima, Manuela ; Filla, Alessandro; Durr, Alexandra; Melegh, Bela; Masciullo, Marcella; Infante, Jon; Giunti, Paola; Neumann, Manuela; de Vries, Jeroen; Almeida, Luís Pereira de ; Rakowicz, Maria; Jacobi, Heike; Schüle, Rebecca; Kaeser, Stephan A.; Kuhle, Jens; Klockgether, Thomas; Schöls, Ludger; Barro, Christian; Hübener-Schmid, Jeannette; Synofzik, MatthisarticleopenAccess
8-Feb-2021Neuropeptide Y (NPY) intranasal delivery alleviates Machado-Joseph diseaseDuarte-Neves, Joana ; Cavadas, Cláudia ; Almeida, Luís Pereira de articleopenAccess
10-Feb-2016Neuropeptide Y gene transfer for neuroprotection in Machado-Joseph DiseaseNeves, Joana Filipa Duarte das doctoralThesisembargoedAccess
2001Neuroprotective Effect of a CNTF-Expressing Lentiviral Vector in the Quinolinic Acid Rat Model of Huntington's DiseaseAlmeida, L. Pereira de ; Zala, D. ; Aebischer, P. ; Déglon, N. articleopenAccess
2016Non-invasive viral-mediated gene therapy for Machado-Joseph diseaseSaraiva, Joana Isabel Rajão masterThesisembargoedAccess
16-Feb-2016Non-viral silencing of Machado-Joseph disease through the systemic routeConceição, Mariana Oliveira doctoralThesisembargoedAccess
2015Novos sistemas para penetração da barreira hematoencefálica : das microbolhas à focagem de ultrassonsMartinho, Luís Miguel LopesmasterThesisembargoedAccess
Jun-2014Oligonucleótidos antisense no tratamento de doenças do sistema nervoso centralAntunes, Telma Cristina HortaotheropenAccess
2015Optogenetics and biotechnology : production and in vitro characterization of Ab-Initio designed channelrhodopsin-2 mutantsPereira, João Miguel CalmeiromasterThesisopenAccess